TRNDS News

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  • Study Presents Clinical, Genetic Landscape of Pompe Disease
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  • A Doctor Tested a New Treatment on Himself, Now it's Saving Other Lives
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  • His daughter has a rare disorder. He’s developing a novel gene therapy.
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  • TRNDS Danielle Edwards Jett Foundation
    TRNDS Speaker Danielle Edwards, Jett Foundation
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  • Benjjamin Schlatka MC10 TRNDS
    TRNDS Speaker Benjamin Schlatka, MC10
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  • Forget Single Genes: CRISPR Now Cuts & Splices Whole Chromosomes
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  • Gene Therapy Developers Issue Principles for Human Genome Editing
    Gene Therapy Developers Issue Principles for Human Genome Editing
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  • TRNDS Nancy Yu RDMD
    TRNDS Speaker Nancy Yu, RDMD
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  • TRNDS, Rachel McMinn, Neurogene
    TRNDS Speaker Rachel McMinn, Neurogene
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  • Gene Linked to Rare Neurological Disorder May Play a Role in Alzheimer’s
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  • FDA Cancer Office Taps Syapse for Real-world Evidence Development
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  • NIH All of Us Project Tops 270,000 Sign-ups
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  • Meet TRNDS 2019 Speaker Traci Schilling, PTC Therapeutics
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  • Netflix's Medical Investigation Docuseries 'Diagnosis'
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  • Ultragenyx Partners with GeneTx to Advance Treatment for Angelman Syndrome
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  • Antisense Drugs for HD, ALS & Prion Could Meet the Need for Brain Treatments
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  • 'Dr. Google' Helps Some Patients Diagnose a Rare Disease
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  • Evidation & Eli Lilly Study Uses Apple Devices, Apps to Predict Cognitive Impairment
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  • HD Patients Prefer Less Invasive, No-Placebo Gene Therapy Trials
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  • TRNDS 2019 speaker Tauna Batiste, BDSRA
    Meet TRNDS Speaker Tauna Batiste
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  • C-Path and NORD Collaborate to Launch Rare Disease Data Platform
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  • Batten Disease Study
    Neurogene Opens Natural History Study of CLN7, CLN5 Diseases at UT Southwestern
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  • Rare Pediatric Disease PRVs: FDA Updates Guidance
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  • PJ Brooks, NCATS, NIH, TRNDS
    Meet TRNDS 2019 Speaker PJ Brooks
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