TRNDS News

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  • FDA Cancer Office Taps Syapse for Real-world Evidence Development
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  • NIH All of Us Project Tops 270,000 Sign-ups
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  • Meet TRNDS 2019 Speaker Traci Schilling, PTC Therapeutics
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  • Netflix's Medical Investigation Docuseries 'Diagnosis'
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  • Ultragenyx Partners with GeneTx to Advance Treatment for Angelman Syndrome
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  • Antisense Drugs for HD, ALS & Prion Could Meet the Need for Brain Treatments
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  • 'Dr. Google' Helps Some Patients Diagnose a Rare Disease
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  • Evidation & Eli Lilly Study Uses Apple Devices, Apps to Predict Cognitive Impairment
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  • HD Patients Prefer Less Invasive, No-Placebo Gene Therapy Trials
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  • TRNDS 2019 speaker Tauna Batiste, BDSRA
    Meet TRNDS Speaker Tauna Batiste
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  • C-Path and NORD Collaborate to Launch Rare Disease Data Platform
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  • Batten Disease Study
    Neurogene Opens Natural History Study of CLN7, CLN5 Diseases at UT Southwestern
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  • Rare Pediatric Disease PRVs: FDA Updates Guidance
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  • PJ Brooks, NCATS, NIH, TRNDS
    Meet TRNDS 2019 Speaker PJ Brooks
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  • Jsyne Gershkowitz, Amicus Therapeutics, TRNDS 2019
    (Podcast) Get to know Jayne Gershkowitz, Chief Patient Advocate at Amicus Therapeutics
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  • Rare Disease Groups Seek Public Support to Renew Newborn Screening Act in Senate
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  • NIH-Funded Project Aims to Build a ‘Google’ for Biomedical Data
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  • Speeding Up Drug Discovery for Brain Diseases
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  • NCATS Director Warns of 'Poorly Understood Public Health Implications of Rare Diseases'
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  • Study refines ALS risk among first-degree relatives of patients with disease
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  • NIH launches 5-year, $10 million study on acute flaccid myelitis
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  • Neurogene Offers Access to Genetic Testing for Lysosomal Storage Disease
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  • New Grants will Accelerate Clinical Trials in Rare Neurological Disorders
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  • Gene Silencing Shows Promise for Treating Two Fatal Neurological Disorders
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