Gene Silencing Shows Promise for Treating Two Fatal Neurological Disorders

University of Rochester Neurology Celebrates 50th Anniversary

International Consensus Addresses Research Bottlenecks to Diagnose Rare Genetic Diseases

TRNDS Interview with Ira Shoulson

Prepare for the Digital Health Revolution

BREAKING: ALS Treatment gets FDA Approval

TRNDS Interview with Dave Jacob

Here’s What Your Future Doctor Visits Could Look Like

PatientsLikeMe Partners with Shire Pharmaceuticals

Interview with Amanda Christini, Blackfynn

AAN 2017; Spinraza Data for SMA Continues to Impress

FDA Approves First Treatment for a Form of Batten Disease

How Multiple Platform Marketing Spread Rare Disease Awareness

TRNDS Interviews Maria Picone

Biotechs take lead in a new push against neurological disorders

MS PATHS: Harnessing Real-Time Patient Data to Reshape MS Care and Research

Interview with Jane Rhodes

The partnership of patient advocacy groups & clinical investigators in the rare diseases clinical research network

The Importance of the Patient Voice

Exclusive Interview with Wendy White

Ethical Issues of Research Recruiting on Social Media

Ethics & Privacy Implications

Rare Diseases: Meeting the Unique Challenges of Orphan Drug Development

The Benefits of Digital Health for Rare Disease Research

Newest ResearchKit Study Focuses on a Rare Disease

Luke Gelinas Interview

Seeker Health Interview