TRNDS | University of Rochester

Technology & Rare Neurological Diseases Symposium

TRNDS is a day-long symposium on emerging novel therapeutic technologies that are creating new and rapidly expanding treatment options for patients with rare neurological disorders.

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TRNDS is hosted and organized by the University of Rochester, a national leader in rare diseases clinical research and therapeutic development.

September 13, 2019

7:30 am – 4:00 pm

University of Rochester
Saunders Research Building
265 Crittenden Boulevard
Rochester, NY 14620


Learn the latest research demonstrating breakthrough health technologies for rare neurological disorders.


Discover new ideas and innovations driving therapy development, clinical trials and clinical research.


Join a community of experts dedicated to accelerating the discovery of new therapies for rare neurological disorders.


TRNDS 2019 speakers include leading clinical researchers, forward-thinking health technology leaders, influential patient advocates, and experts in regulatory science. Confirmed speakers include:

Derek Bowen VP Business Development & Strategy, Blackfynn

PJ Brooks Program Director, Office of Rare Diseases Research, National Center for Advancing Translational Sciences, NIH

Wilson Bryan Director, Office of Tissues & Advanced Therapies, Center for Biologics Evaluation & Research, FDA

Tanya Fischer Global Project Head, Sanofi-Genzyme

Jayne Gershkowitz Chief Patient Advocate, Amicus Therapeutics

David Jacoby VP, Head of Clinical Science, BioMarin Pharmaceuticals

Rachel McMinn President & CEO, Neurogene, Inc.

Nancy Yu Co-Founder & CEO, RDMD

Timothy Yu Asst. Prof., Division of Genetics & Genomics, Harvard Medical School

Dina Zand Medical Officer, Center for Drug Evaluation & Research, FDA


TRNDS 2019 program will focus on emerging gene therapy approaches, a new era in enzyme replacement therapy, the future of newborn screening, and novel tools and technologies contributing to the modernization of clinical research. Topics include:

Emerging approaches to treating serious, rare neurological conditions

Personalized medicine in a neurological disease framework

Development of paths to early diagnosis

Use of novel technologies to facilitate high quality, efficient clinical research studies

Ethical considerations in the modernization of clinical trials and development of new therapies

Past Speakers

Regional and national leaders in rare diseases, health technologies and clinical trials


Stay informed of current rare disease news and TRNDS updates

  • Gene Silencing Shows Promise for Treating Two Fatal Neurological Disorders
  • International Consensus Addresses Research Bottlenecks to Diagnose Rare Genetic Diseases
  • TRNDS Interview with Ira Shoulson
  • University of Rochester Neurology Celebrates 50th Anniversary

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